Institutional Research Information Service
UCL Logo
Please report any queries concerning the funding data grouped in the sections named "Externally Awarded" or "Internally Disbursed" (shown on the profile page) to your Research Finance Administrator. Your can find your Research Finance Administrator at https://www.ucl.ac.uk/finance/research/rs-contacts.php by entering your department
Please report any queries concerning the student data shown on the profile page to:

Email: portico-services@ucl.ac.uk

Help Desk: http://www.ucl.ac.uk/ras/portico/helpdesk
Gene Therapy Group
Gene therapy is the insertion of nucleic acids into cells of an organism in order to change or correct its phenotype with the ultimate purpose of treating disease. Whereas traditional drugs act by direct and transient modification of a biological target, the purpose of gene therapy is to reprogram cells. Clinical studies have now demonstrated biological responses or efficacy following gene therapy in patients with genetic diseases affecting the immune system, skin, blood clotting or retina. Positive data have also been reported in patients with AIDS, melanoma and Parkinson disease. Although these studies clearly indicate that gene therapy will be a part of molecular medicine practice in the near future, they also reveal difficulties, limitations and toxicities that require attention.
8 Researchers
 More search options
University College London - Gower Street - London - WC1E 6BT Tel:+44 (0)20 7679 2000

© UCL 1999–2011

Search by